Table of Contents 1 Report Overview 1.1 Study Scope 1.2 Key Market Segments 1.3 Players Covered: Ranking by Gene Therapy for Inherited Genetic Disorders Revenue 1.4 Market Analysis by Type 1.4.1 Global Gene Therapy for Inherited Genetic Disorders Market Size Growth Rate by Type: 2020 VS 2026 1.4.2 Eye Disorders 1.4.3 Hematological Disorders 1.4.4 Central Nervous System Disorders 1.4.5 Muscular Disorders 1.4.6 Others 1.5 Market by Application 1.5.1 Global Gene Therapy for Inherited Genetic Disorders Market Share by Application: 2020 VS 2026 1.5.2 Hospital 1.5.3 Clinic 1.5.4 Research Institute 1.5.5 Others 1.6 Study Objectives 1.7 Years Considered 2 Global Growth Trends by Regions 2.1 Gene Therapy for Inherited Genetic Disorders Market Perspective (2015-2026) 2.2 Gene Therapy for Inherited Genetic Disorders Growth Trends by Regions 2.2.1 Gene Therapy for Inherited Genetic Disorders Market Size by Regions: 2015 VS 2020 VS 2026 2.2.2 Gene Therapy for Inherited Genetic Disorders Historic Market Share by Regions (2015-2020) 2.2.3 Gene Therapy for Inherited Genetic Disorders Forecasted Market Size by Regions (2021-2026) 2.3 Industry Trends and Growth Strategy 2.3.1 Market Top Trends 2.3.2 Market Drivers 2.3.3 Market Challenges 2.3.4 Porter’s Five Forces Analysis 2.3.5 Gene Therapy for Inherited Genetic Disorders Market Growth Strategy 2.3.6 Primary Interviews with Key Gene Therapy for Inherited Genetic Disorders Players (Opinion Leaders) 3 Competition Landscape by Key Players 3.1 Global Top Gene Therapy for Inherited Genetic Disorders Players by Market Size 3.1.1 Global Top Gene Therapy for Inherited Genetic Disorders Players by Revenue (2015-2020) 3.1.2 Global Gene Therapy for Inherited Genetic Disorders Revenue Market Share by Players (2015-2020) 3.1.3 Global Gene Therapy for Inherited Genetic Disorders Market Share by Company Type (Tier 1, Tier 2 and Tier 3) 3.2 Global Gene Therapy for Inherited Genetic Disorders Market Concentration Ratio 3.2.1 Global Gene Therapy for Inherited Genetic Disorders Market Concentration Ratio (CR5 and HHI) 3.2.2 Global Top 10 and Top 5 Companies by Gene Therapy for Inherited Genetic Disorders Revenue in 2019 3.3 Gene Therapy for Inherited Genetic Disorders Key Players Head office and Area Served 3.4 Key Players Gene Therapy for Inherited Genetic Disorders Product Solution and Service 3.5 Date of Enter into Gene Therapy for Inherited Genetic Disorders Market 3.6 Mergers & Acquisitions, Expansion Plans 4 Breakdown Data by Type (2015-2026) 4.1 Global Gene Therapy for Inherited Genetic Disorders Historic Market Size by Type (2015-2020) 4.2 Global Gene Therapy for Inherited Genetic Disorders Forecasted Market Size by Type (2021-2026) 5 Gene Therapy for Inherited Genetic Disorders Breakdown Data by Application (2015-2026) 5.1 Global Gene Therapy for Inherited Genetic Disorders Market Size by Application (2015-2020) 5.2 Global Gene Therapy for Inherited Genetic Disorders Forecasted Market Size by Application (2021-2026) 6 North America 6.1 North America Gene Therapy for Inherited Genetic Disorders Market Size (2015-2020) 6.2 Gene Therapy for Inherited Genetic Disorders Key Players in North America (2019-2020) 6.3 North America Gene Therapy for Inherited Genetic Disorders Market Size by Type (2015-2020) 6.4 North America Gene Therapy for Inherited Genetic Disorders Market Size by Application (2015-2020) 7 Europe 7.1 Europe Gene Therapy for Inherited Genetic Disorders Market Size (2015-2020) 7.2 Gene Therapy for Inherited Genetic Disorders Key Players in Europe (2019-2020) 7.3 Europe Gene Therapy for Inherited Genetic Disorders Market Size by Type (2015-2020) 7.4 Europe Gene Therapy for Inherited Genetic Disorders Market Size by Application (2015-2020) 8 China 8.1 China Gene Therapy for Inherited Genetic Disorders Market Size (2015-2020) 8.2 Gene Therapy for Inherited Genetic Disorders Key Players in China (2019-2020) 8.3 China Gene Therapy for Inherited Genetic Disorders Market Size by Type (2015-2020) 8.4 China Gene Therapy for Inherited Genetic Disorders Market Size by Application (2015-2020) 9 Japan 9.1 Japan Gene Therapy for Inherited Genetic Disorders Market Size (2015-2020) 9.2 Gene Therapy for Inherited Genetic Disorders Key Players in Japan (2019-2020) 9.3 Japan Gene Therapy for Inherited Genetic Disorders Market Size by Type (2015-2020) 9.4 Japan Gene Therapy for Inherited Genetic Disorders Market Size by Application (2015-2020) 10 Southeast Asia 10.1 Southeast Asia Gene Therapy for Inherited Genetic Disorders Market Size (2015-2020) 10.2 Gene Therapy for Inherited Genetic Disorders Key Players in Southeast Asia (2019-2020) 10.3 Southeast Asia Gene Therapy for Inherited Genetic Disorders Market Size by Type (2015-2020) 10.4 Southeast Asia Gene Therapy for Inherited Genetic Disorders Market Size by Application (2015-2020) 11 India 11.1 India Gene Therapy for Inherited Genetic Disorders Market Size (2015-2020) 11.2 Gene Therapy for Inherited Genetic Disorders Key Players in India (2019-2020) 11.3 India Gene Therapy for Inherited Genetic Disorders Market Size by Type (2015-2020) 11.4 India Gene Therapy for Inherited Genetic Disorders Market Size by Application (2015-2020) 12 Central & South America 12.1 Central & South America Gene Therapy for Inherited Genetic Disorders Market Size (2015-2020) 12.2 Gene Therapy for Inherited Genetic Disorders Key Players in Central & South America (2019-2020) 12.3 Central & South America Gene Therapy for Inherited Genetic Disorders Market Size by Type (2015-2020) 12.4 Central & South America Gene Therapy for Inherited Genetic Disorders Market Size by Application (2015-2020) 13Key Players Profiles 13.1 BioMarin Pharmaceutical Inc. 13.1.1 BioMarin Pharmaceutical Inc. Company Details 13.1.2 BioMarin Pharmaceutical Inc. Business Overview and Its Total Revenue 13.1.3 BioMarin Pharmaceutical Inc. Gene Therapy for Inherited Genetic Disorders Introduction 13.1.4 BioMarin Pharmaceutical Inc. Revenue in Gene Therapy for Inherited Genetic Disorders Business (2015-2020)) 13.1.5 BioMarin Pharmaceutical Inc. Recent Development 13.2 bluebird bio Inc. 13.2.1 bluebird bio Inc. Company Details 13.2.2 bluebird bio Inc. Business Overview and Its Total Revenue 13.2.3 bluebird bio Inc. Gene Therapy for Inherited Genetic Disorders Introduction 13.2.4 bluebird bio Inc. Revenue in Gene Therapy for Inherited Genetic Disorders Business (2015-2020) 13.2.5 bluebird bio Inc. Recent Development 13.3 Novartis AG 13.3.1 Novartis AG Company Details 13.3.2 Novartis AG Business Overview and Its Total Revenue 13.3.3 Novartis AG Gene Therapy for Inherited Genetic Disorders Introduction 13.3.4 Novartis AG Revenue in Gene Therapy for Inherited Genetic Disorders Business (2015-2020) 13.3.5 Novartis AG Recent Development 13.4 Orchard Therapeutics Plc 13.4.1 Orchard Therapeutics Plc Company Details 13.4.2 Orchard Therapeutics Plc Business Overview and Its Total Revenue 13.4.3 Orchard Therapeutics Plc Gene Therapy for Inherited Genetic Disorders Introduction 13.4.4 Orchard Therapeutics Plc Revenue in Gene Therapy for Inherited Genetic Disorders Business (2015-2020) 13.4.5 Orchard Therapeutics Plc Recent Development 13.5 Spark Therapeutics Inc. 13.5.1 Spark Therapeutics Inc. Company Details 13.5.2 Spark Therapeutics Inc. Business Overview and Its Total Revenue 13.5.3 Spark Therapeutics Inc. Gene Therapy for Inherited Genetic Disorders Introduction 13.5.4 Spark Therapeutics Inc. Revenue in Gene Therapy for Inherited Genetic Disorders Business (2015-2020) 13.5.5 Spark Therapeutics Inc. Recent Development 14Analyst's Viewpoints/Conclusions 15Appendix 15.1 Research Methodology 15.1.1 Methodology/Research Approach 15.1.2 Data Source 15.2 Disclaimer 15.3 Author Details

List of Tables Table 1. Gene Therapy for Inherited Genetic Disorders Key Market Segments Table 2. Key Players Covered: Ranking by Gene Therapy for Inherited Genetic Disorders Revenue Table 3. Ranking of Global Top Gene Therapy for Inherited Genetic Disorders Manufacturers by Revenue (US$ Million) in 2019 Table 4. Global Gene Therapy for Inherited Genetic Disorders Market Size Growth Rate by Type (US$ Million): 2020 VS 2026 Table 5. Key Players of Eye Disorders Table 6. Key Players of Hematological Disorders Table 7. Key Players of Central Nervous System Disorders Table 8. Key Players of Muscular Disorders Table 9. Key Players of Others Table 10. Global Gene Therapy for Inherited Genetic Disorders Market Size Growth by Application (US$ Million): 2020 VS 2026 Table 11. Global Gene Therapy for Inherited Genetic Disorders Market Size by Regions (US$ Million): 2020 VS 2026 Table 12. Global Gene Therapy for Inherited Genetic Disorders Market Size by Regions (2015-2020) (US$ Million) Table 13. Global Gene Therapy for Inherited Genetic Disorders Market Share by Regions (2015-2020) Table 14. Global Gene Therapy for Inherited Genetic Disorders Forecasted Market Size by Regions (2021-2026) (US$ Million) Table 15. Global Gene Therapy for Inherited Genetic Disorders Market Share by Regions (2021-2026) Table 16. Market Top Trends Table 17. Key Drivers: Impact Analysis Table 18. Key Challenges Table 19. Gene Therapy for Inherited Genetic Disorders Market Growth Strategy Table 20. Main Points Interviewed from Key Gene Therapy for Inherited Genetic Disorders Players Table 21. Global Gene Therapy for Inherited Genetic Disorders Revenue by Players (2015-2020) (Million US$) Table 22. Global Gene Therapy for Inherited Genetic Disorders Market Share by Players (2015-2020) Table 23. Global Top Gene Therapy for Inherited Genetic Disorders Players by Company Type (Tier 1, Tier 2 and Tier 3) (based on the Revenue in Gene Therapy for Inherited Genetic Disorders as of 2019) Table 24. Global Gene Therapy for Inherited Genetic Disorders by Players Market Concentration Ratio (CR5 and HHI) Table 25. Key Players Headquarters and Area Served Table 26. Key Players Gene Therapy for Inherited Genetic Disorders Product Solution and Service Table 27. Date of Enter into Gene Therapy for Inherited Genetic Disorders Market Table 28. Mergers & Acquisitions, Expansion Plans Table 29. Global Gene Therapy for Inherited Genetic Disorders Market Size by Type (2015-2020) (Million US$) Table 30. Global Gene Therapy for Inherited Genetic Disorders Market Size Share by Type (2015-2020) Table 31. Global Gene Therapy for Inherited Genetic Disorders Revenue Market Share by Type (2021-2026) Table 32. Global Gene Therapy for Inherited Genetic Disorders Market Size Share by Application (2015-2020) Table 33. Global Gene Therapy for Inherited Genetic Disorders Market Size by Application (2015-2020) (Million US$) Table 34. Global Gene Therapy for Inherited Genetic Disorders Market Size Share by Application (2021-2026) Table 35. North America Key Players Gene Therapy for Inherited Genetic Disorders Revenue (2019-2020) (Million US$) Table 36. North America Key Players Gene Therapy for Inherited Genetic Disorders Market Share (2019-2020) Table 37. North America Gene Therapy for Inherited Genetic Disorders Market Size by Type (2015-2020) (Million US$) Table 38. North America Gene Therapy for Inherited Genetic Disorders Market Share by Type (2015-2020) Table 39. North America Gene Therapy for Inherited Genetic Disorders Market Size by Application (2015-2020) (Million US$) Table 40. North America Gene Therapy for Inherited Genetic Disorders Market Share by Application (2015-2020) Table 41. Europe Key Players Gene Therapy for Inherited Genetic Disorders Revenue (2019-2020) (Million US$) Table 42. Europe Key Players Gene Therapy for Inherited Genetic Disorders Market Share (2019-2020) Table 43. Europe Gene Therapy for Inherited Genetic Disorders Market Size by Type (2015-2020) (Million US$) Table 44. Europe Gene Therapy for Inherited Genetic Disorders Market Share by Type (2015-2020) Table 45. Europe Gene Therapy for Inherited Genetic Disorders Market Size by Application (2015-2020) (Million US$) Table 46. Europe Gene Therapy for Inherited Genetic Disorders Market Share by Application (2015-2020) Table 47. China Key Players Gene Therapy for Inherited Genetic Disorders Revenue (2019-2020) (Million US$) Table 48. China Key Players Gene Therapy for Inherited Genetic Disorders Market Share (2019-2020) Table 49. China Gene Therapy for Inherited Genetic Disorders Market Size by Type (2015-2020) (Million US$) Table 50. China Gene Therapy for Inherited Genetic Disorders Market Share by Type (2015-2020) Table 51. China Gene Therapy for Inherited Genetic Disorders Market Size by Application (2015-2020) (Million US$) Table 52. China Gene Therapy for Inherited Genetic Disorders Market Share by Application (2015-2020) Table 53. Japan Key Players Gene Therapy for Inherited Genetic Disorders Revenue (2019-2020) (Million US$) Table 54. Japan Key Players Gene Therapy for Inherited Genetic Disorders Market Share (2019-2020) Table 55. Japan Gene Therapy for Inherited Genetic Disorders Market Size by Type (2015-2020) (Million US$) Table 56. Japan Gene Therapy for Inherited Genetic Disorders Market Share by Type (2015-2020) Table 57. Japan Gene Therapy for Inherited Genetic Disorders Market Size by Application (2015-2020) (Million US$) Table 58. Japan Gene Therapy for Inherited Genetic Disorders Market Share by Application (2015-2020) Table 59. Southeast Asia Key Players Gene Therapy for Inherited Genetic Disorders Revenue (2019-2020) (Million US$) Table 60. Southeast Asia Key Players Gene Therapy for Inherited Genetic Disorders Market Share (2019-2020) Table 61. Southeast Asia Gene Therapy for Inherited Genetic Disorders Market Size by Type (2015-2020) (Million US$) Table 62. Southeast Asia Gene Therapy for Inherited Genetic Disorders Market Share by Type (2015-2020) Table 63. Southeast Asia Gene Therapy for Inherited Genetic Disorders Market Size by Application (2015-2020) (Million US$) Table 64. Southeast Asia Gene Therapy for Inherited Genetic Disorders Market Share by Application (2015-2020) Table 65. India Key Players Gene Therapy for Inherited Genetic Disorders Revenue (2019-2020) (Million US$) Table 66. India Key Players Gene Therapy for Inherited Genetic Disorders Market Share (2019-2020) Table 67. India Gene Therapy for Inherited Genetic Disorders Market Size by Type (2015-2020) (Million US$) Table 68. India Gene Therapy for Inherited Genetic Disorders Market Share by Type (2015-2020) Table 69. India Gene Therapy for Inherited Genetic Disorders Market Size by Application (2015-2020) (Million US$) Table 70. India Gene Therapy for Inherited Genetic Disorders Market Share by Application (2015-2020) Table 71. Central & South America Key Players Gene Therapy for Inherited Genetic Disorders Revenue (2019-2020) (Million US$) Table 72. Central & South America Key Players Gene Therapy for Inherited Genetic Disorders Market Share (2019-2020) Table 73. Central & South America Gene Therapy for Inherited Genetic Disorders Market Size by Type (2015-2020) (Million US$) Table 74. Central & South America Gene Therapy for Inherited Genetic Disorders Market Share by Type (2015-2020) Table 75. Central & South America Gene Therapy for Inherited Genetic Disorders Market Size by Application (2015-2020) (Million US$) Table 76. Central & South America Gene Therapy for Inherited Genetic Disorders Market Share by Application (2015-2020) Table 77. BioMarin Pharmaceutical Inc. Company Details Table 78. BioMarin Pharmaceutical Inc. Business Overview Table 79. BioMarin Pharmaceutical Inc. Product Table 80. BioMarin Pharmaceutical Inc. Revenue in Gene Therapy for Inherited Genetic Disorders Business (2015-2020) (Million US$) Table 81. BioMarin Pharmaceutical Inc. Recent Development Table 82. bluebird bio Inc. Company Details Table 83. bluebird bio Inc. Business Overview Table 84. bluebird bio Inc. Product Table 85. bluebird bio Inc. Revenue in Gene Therapy for Inherited Genetic Disorders Business (2015-2020) (Million US$) Table 86. bluebird bio Inc. Recent Development Table 87. Novartis AG Company Details Table 88. Novartis AG Business Overview Table 89. Novartis AG Product Table 90. Novartis AG Revenue in Gene Therapy for Inherited Genetic Disorders Business (2015-2020) (Million US$) Table 91. Novartis AG Recent Development Table 92. Orchard Therapeutics Plc Company Details Table 93. Orchard Therapeutics Plc Business Overview Table 94. Orchard Therapeutics Plc Product Table 95. Orchard Therapeutics Plc Revenue in Gene Therapy for Inherited Genetic Disorders Business (2015-2020) (Million US$) Table 96. Orchard Therapeutics Plc Recent Development Table 97. Spark Therapeutics Inc. Company Details Table 98. Spark Therapeutics Inc. Business Overview Table 99. Spark Therapeutics Inc. Product Table 100. Spark Therapeutics Inc. Revenue in Gene Therapy for Inherited Genetic Disorders Business (2015-2020) (Million US$) Table 101. Spark Therapeutics Inc. Recent Development Table 102. Research Programs/Design for This Report Table 103. Key Data Information from Secondary Sources Table 104. Key Data Information from Primary Sources List of Figures Figure 1. Global Gene Therapy for Inherited Genetic Disorders Market Share by Type: 2020 VS 2026 Figure 2. Eye Disorders Features Figure 3. Hematological Disorders Features Figure 4. Central Nervous System Disorders Features Figure 5. Muscular Disorders Features Figure 6. Others Features Figure 7. Global Gene Therapy for Inherited Genetic Disorders Market Share by Application: 2020 VS 2026 Figure 8. Hospital Case Studies Figure 9. Clinic Case Studies Figure 10. Research Institute Case Studies Figure 11. Others Case Studies Figure 12. Gene Therapy for Inherited Genetic Disorders Report Years Considered Figure 13. Global Gene Therapy for Inherited Genetic Disorders Market Size YoY Growth 2015-2026 (US$ Million) Figure 14. Global Gene Therapy for Inherited Genetic Disorders Market Share by Regions: 2020 VS 2026 Figure 15. Global Gene Therapy for Inherited Genetic Disorders Market Share by Regions (2021-2026) Figure 16. Porter's Five Forces Analysis Figure 17. Global Gene Therapy for Inherited Genetic Disorders Market Share by Players in 2019 Figure 18. Global Top Gene Therapy for Inherited Genetic Disorders Players by Company Type (Tier 1, Tier 2 and Tier 3) (based on the Revenue in Gene Therapy for Inherited Genetic Disorders as of 2019 Figure 19. The Top 10 and 5 Players Market Share by Gene Therapy for Inherited Genetic Disorders Revenue in 2019 Figure 20. North America Gene Therapy for Inherited Genetic Disorders Market Size YoY Growth (2015-2020) (Million US$) Figure 21. Europe Gene Therapy for Inherited Genetic Disorders Market Size YoY Growth (2015-2020) (Million US$) Figure 22. China Gene Therapy for Inherited Genetic Disorders Market Size YoY Growth (2015-2020) (Million US$) Figure 23. Japan Gene Therapy for Inherited Genetic Disorders Market Size YoY Growth (2015-2020) (Million US$) Figure 24. Southeast Asia Gene Therapy for Inherited Genetic Disorders Market Size YoY Growth (2015-2020) (Million US$) Figure 25. India Gene Therapy for Inherited Genetic Disorders Market Size YoY Growth (2015-2020) (Million US$) Figure 26. Central & South America Gene Therapy for Inherited Genetic Disorders Market Size YoY Growth (2015-2020) (Million US$) Figure 27. BioMarin Pharmaceutical Inc. Total Revenue (US$ Million): 2019 Compared with 2018 Figure 28. BioMarin Pharmaceutical Inc. Revenue Growth Rate in Gene Therapy for Inherited Genetic Disorders Business (2015-2020) Figure 29. bluebird bio Inc. Total Revenue (US$ Million): 2019 Compared with 2018 Figure 30. bluebird bio Inc. Revenue Growth Rate in Gene Therapy for Inherited Genetic Disorders Business (2015-2020) Figure 31. Novartis AG Total Revenue (US$ Million): 2019 Compared with 2018 Figure 32. Novartis AG Revenue Growth Rate in Gene Therapy for Inherited Genetic Disorders Business (2015-2020) Figure 33. Orchard Therapeutics Plc Total Revenue (US$ Million): 2019 Compared with 2018 Figure 34. Orchard Therapeutics Plc Revenue Growth Rate in Gene Therapy for Inherited Genetic Disorders Business (2015-2020) Figure 35. Spark Therapeutics Inc. Total Revenue (US$ Million): 2019 Compared with 2018 Figure 36. Spark Therapeutics Inc. Revenue Growth Rate in Gene Therapy for Inherited Genetic Disorders Business (2015-2020) Figure 37. Bottom-up and Top-down Approaches for This Report Figure 38. Data Triangulation Figure 39. Key Executives Interviewed

BioMarin Pharmaceutical Inc. bluebird bio Inc. Novartis AG Orchard Therapeutics Plc Spark Therapeutics Inc.