Global Duchenne Muscular Dystrophy Therapeutics Market By Drug (Translarna, Emflaza, EXONDYS 51), By Therapeutic Approach (Steroid Therapy, Exon Skipping, Mutation Suppression) Forecast to 2022
SKU ID :RNCOS-10849042 | Published Date: 12-May-2017 | No. of pages: 100Description
TOC
1. Analyst View
2. Research Methodology
3. Duchenne Muscular Dystrophy (DMD): An Overview
4. Market Dynamics
4.1 Market Drivers
4.1.1 Growing Prevalence of Duchenne Muscular Dystrophy
4.1.2 Rising Acceptance of Duchenne Muscular Dystrophy Drugs in the Market
4.1.3 Increasing Funding Support & Grants
4.1.4 Increasing Awareness
4.1.5 Robust and Opportunistic Pipeline
4.2 Restraints
4.2.1 Pediatric Neuromuscular Disease
4.2.2 Lack of Disease History and Research Participants
4.2.3 Diagnosis and Management of Duchenne Muscular Dystrophy in Developing Countries
4.2.4 High Cost of Care
4.3 Opportunities
4.3.1 PPMO: Next Generation Antisense Platform
4.3.2 Growing Market Opportunity in Emerging Countries
4.3.3 High Unmet Need for an Effective Disease Modifying Therapy
4.3.4 Gene Therapy
4.3.5 Utrophin Modulation
4.3.6 Biomarkers for Duchenne Muscular Dystophy
5. Global Duchenne Muscular Dystrophy Therapeutics Market Outlook 2022
6. Approved Drugs
6.1 Emflaza (deflazacort)
6.2 EXONDYS 51 (eteplirsen)
6.3 Translarna (ataluren)
7. Market Segmentation by Therapeutic Approach
7.1 Mutation Suppression
7.2 Steroid Therapy
7.3 Exon Skipping Therapy
8. Market Segmentation by Geography
8.1 Europe
8.2 North America
8.3 Asia Pacific
9. Clinical Trial Assessment & Pipeline Analysis
9.1 Clinical Trials
9.1.1 By Geography
9.1.2 By Clinical Trial Phase
9.1.3 By Key Players
9.2 Pipeline Analysis
10. Industry Trends and Developments
10.1 Administration of Corticosteroids
10.2 Collaboration amongst Industry Players and Non-Industry Participants
10.3 Exon-Skipping Technology Crowding the DMD Therapeutics Industry
10.4 Carrier Screening for Duchenne Muscular Dystrophy
11. Strategic Alliances
12. Competitive Landscape
13. Key Player Analysis
13.1 Marathon Pharmaceuticals, LLC
13.2 PTC Therapeutics, Inc.
13.3 Sarepta Therapeutics, Inc.
13.4 ITALFARMACO S.p.A.
13.5 Santhera Pharmaceuticals
13.6 Bristol-Myers Squibb
13.7 ReveraGen BioPharma, Inc.
13.8 Catabasis Pharmaceuticals, Inc.
13.9 FibroGen, Inc.
13.10 NS Pharma, Inc.
13.11 Pfizer
13.12 Summit Therapeutics plc
13.13 Taiho Pharmaceutical Co., Ltd. (Division of Otsuka Holdings Co. Ltd.)
14. Future Outlook
List of Figures:
Figure 5-1: Global - Duchenne Muscular Dystrophy Therapeutics Market (Million US$), 2016-2022
Figure 6-1: Global - Sales of EXONDYS 51 (Million US$), 2016
Figure 6-2: Global - Sales of Translarna (Million US$), 2014-2017
Figure 7-1: Global - Duchenne Muscular Dystrophy Therapeutics Market by Therapeutic Approach (%), 2016
Figure 7-2: Global - Mutation Suppression Market for Duchenne Muscular Dystrophy (Million US$), 2016-2022
Figure 7-3: Global - Steroid Therapy Market for Duchenne Muscular Dystrophy (Million US$), 2016-2022
Figure 7-4: Global - Exon Skipping Therapy Market for Duchenne Muscular Dystrophy (Million US$), 2016-2022
Figure 8-1: Global - Duchenne Muscular Dystrophy Therapeutics Market by Geography (%), 2016
Figure 8-2: Europe - Duchenne Muscular Dystrophy Therapeutics Market (Million US$), 2016-2022
Figure 8-3: North America - Duchenne Muscular Dystrophy Therapeutics Market (Million US$), 2016-2022
Figure 8-4: Asia Pacific - Duchenne Muscular Dystrophy Therapeutics Market (Million US$), 2016-2022
Figure 9-1: Global - Duchenne Muscular Dystrophy Clinical Trials by Countries till April, 2017
Figure 9-2: Global - Duchenne Muscular Dystrophy Clinical Trials by Phase till April, 2017
Figure 9-3: Global - Duchenne Muscular Dystrophy Clinical Trials by Key Players till April, 2017
Figure 10-1: Exon Skipping Clinical Candidates
Figure 12-1: Global - Share of Major Players in Duchenne Muscular Dystrophy Therapeutics Market (%), 2016
Figure 13-1: PTC Therapeutics, Inc. - Revenue by Geography (%), 2016
Figure 13-2: Santhera Pharmaceuticals - Revenue by Business Segments (%), 2015
Figure 13-3: Santhera Pharmaceuticals - Revenue by Geography (%), 2015
Figure 13-4: Bristol Myers Squibb - Revenue by Business Segments (%), 2015
Figure 13-5: Bristol Myers Squibb - Revenue by Geography (%), 2015
Figure 13-6: FibroGen, Inc. - Revenue by Geography (%), 2016
Figure 13-7: Pfizer Inc. - Revenue by Business Segments (%), 2016
Figure 13-8: Pfizer Inc. - Revenue by Geography (%), 2016
List of Tables:
Table 4-1: Grants for Duchenne Muscular Dystrophy
Table 4-2: Per-Patient Annual Costs of DMD, 2012
Table 6-1: Ongoing Trials for Emflaza
Table 6-2: Ongoing Trials for EXONDYS 51
Table 6-3: Ongoing Trials for Translarna
Table 7-1: Disease-Modifying Therapies for Duchenne Muscular Dystrophy
Table 9-1: Global Duchenne Muscular Dystrophy Therapeutics Pipeline
Table 13-1: Marathon Pharmaceuticals, LLC – Commercialized Duchenne Muscular Dystrophy Products
Table 13-2: PTC Therapeutics, Inc. - Key Financials (Million US$), 2014-2016
Table 13-3: PTC Therapeutics, Inc. – Commercialized Duchenne Muscular Dystrophy Products
Table 13-4: PTC Therapeutics, Inc. – Product Pipeline
Table 13-5: Sarepta Therapeutics, Inc. - Key Financials (Million US$), 2014-2016
Table 13-6: Sarepta Therapeutics, Inc. – Commercialized Duchenne Muscular Dystrophy Products
Table 13-7: Sarepta Therapeutics, Inc. – Product Pipeline
Table 13-8: ITALFARMACO S.p.A. – Product Pipeline
Table 13-9: Santhera Pharmaceuticals - Key Financials (Million US$), 2013-2015
Table 13-10: Santhera Pharmaceuticals – Product Pipeline
Table 13-11: Bristol Myers Squibb - Key Financials (Million US$), 2013-2015
Table 13-12: Bristol Myers Squibb – Product Pipeline
Table 13-13: ReveraGen BioPharma, Inc. – Product Pipeline
Table 13-14: Catabasis Pharmaceuticals, Inc. - Key Financials (Million US$), 2014-2016
Table 13-15: Catabasis Pharmaceuticals, Inc. – Product Pipeline
Table 13-16: FibroGen, Inc. - Key Financials (Million US$), 2014-2016
Table 13-17: FibroGen, Inc. – Product Pipeline
Table 13-18: NS Pharma, Inc. – Product Pipeline
Table 13-19: Pfizer Inc. - Key Financials (Million US$), 2014-2016
Table 13-20: Pfizer Inc. – Product Pipeline
Table 13-21: Summit Therapeutics plc – Product Pipeline
Table 13-22: Taiho Pharmaceutical Co., Ltd. - Key Financials (Million US$), 2014-2016
Table 13-23: Taiho Pharmaceutical Co., Ltd. – Product Pipeline
Tables & Figures
Companies
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